subretinal gene therapy
Showing 1 - 25 of >10,000
Retinitis Pigmentosa Trial in Tuebingen (subretinal injection of rAAV.hPDE6A)
Active, not recruiting
- Retinitis Pigmentosa
- subretinal injection of rAAV.hPDE6A
-
Tuebingen, GermanyUniversitätsklinikum Tübingen, Department für Augenheilkunde
Dec 7, 2022
Neovascular Age-related Macular Degeneration Trial (RRG001)
Not yet recruiting
- Neovascular Age-related Macular Degeneration
- (no location specified)
Nov 15, 2023
Biallelic RPE65 Mutation-associated Retinal Dystrophy Trial in Beijing (FT-001 Low Dose, FT-001 Mid Dose, FT-001 High Dose)
Recruiting
- Biallelic RPE65 Mutation-associated Retinal Dystrophy
- FT-001 Low Dose
- +2 more
-
Beijing, Beijing, ChinaPeking Union Medical College Hospital
May 11, 2023
Achromatopsia Trial in Tuebingen (rAAV.hCNGA3)
Recruiting
- Achromatopsia
-
Tuebingen, GermanyUniversity Hospital Tuebingen, Center for Ophthalmology
Dec 7, 2022
Retinitis Pigmentosa Trial in Stockholm (CPK850)
Recruiting
- Retinitis Pigmentosa
- CPK850
-
Stockholm, SwedenNovartis Investigative Site
May 16, 2022
LCA5 Trial (AAV8.hLCA5)
Not yet recruiting
- LCA5
- AAV8.hLCA5
- (no location specified)
Nov 22, 2022
Bietti's Crystalline Dystrophy Trial in Beijing (Gene Replacement Therapy by rAAV2/8-hCYP4V2)
Recruiting
- Bietti's Crystalline Dystrophy
- Gene Replacement Therapy by rAAV2/8-hCYP4V2
-
Beijing, Beijing, ChinaBeijing Tongren Hospital
May 6, 2021
Amaurosis of Leber, Retinal Diseases Trial in Gainesville, Philadelphia (rAAV2-CBSB-hRPE65)
Active, not recruiting
- Amaurosis of Leber
- Retinal Diseases
- rAAV2-CBSB-hRPE65
-
Gainesville, Florida
- +1 more
Dec 13, 2021
Age-Related Macular Degeneration Trial in Toronto (NG101 AAV gene therapy)
Not yet recruiting
- Age-Related Macular Degeneration
- NG101 AAV gene therapy
-
Toronto, Ontario, CanadaVitreous Retina Macula Specialists of Toronto
Aug 2, 2023
Neovascular Age-related Macular Degeneration, Wet Macular Degeneration, Wet Age-related Macular Degeneration Trial in United
Recruiting
- Neovascular Age-related Macular Degeneration
- +2 more
- RGX-314
-
Phoenix, Arizona
- +12 more
Oct 12, 2021
Retinal Disease, Retinitis Pigmentosa Trial in Riyadh (Subretinal administration of rAAV2-VMD2-hMERTKRecombinant
Completed
- Retinal Disease
- Retinitis Pigmentosa
- Subretinal administration of rAAV2-VMD2-hMERTKRecombinant Adeno-Associated Virus
-
Riyadh, Saudi ArabiaKing Khaled Eye Specialist Hospital
Jan 25, 2022
Retinitis Pigmentosa Trial in Nantes (AAV2/5-hPDE6B)
Active, not recruiting
- Retinitis Pigmentosa
- AAV2/5-hPDE6B
-
Nantes, FranceClinique Ophtalmologique, CHU de Nantes
Feb 28, 2022
Age-Related Macular Degeneration Trial in Beijing (KH631)
Not yet recruiting
- Age-Related Macular Degeneration
-
Beijing, ChinaBeijing Tongren Hospital, Capital Medical University
Jan 3, 2023
To Evaluate the Scaling Clinical Study of AAV2-RPE65 Gene Therapy Agent (LX101) in Patients With Congenital Amaurosis (LCA)
Not yet recruiting
- To Evaluate the Scaling Clinical Study of AAV2-RPE65 Gene Therapy Agent (LX101) in Patients With Congenital Amaurosis (LCA)
- (no location specified)
Aug 29, 2023
Leber Congenital Amaurosis Trial in Shanghai (HG004)
Recruiting
- Leber Congenital Amaurosis
- HG004
-
Shanghai, Shanghai, ChinaXinhua Hospital affiliated with Shanghai Jiao Tong University Sc
Sep 26, 2023
Subjects Who Received Voretigene Neparvovec-rzyl (AAV2-hRPE65v2)
Active, not recruiting
- Inherited Retinal Dystrophy Due to RPE65 Mutations
- AAV2-hRPE65v2
- (no location specified)
Dec 9, 2021
X-linked Retinoschisis Trial (ATSN-201)
Not yet recruiting
- X-linked Retinoschisis
- ATSN-201
- (no location specified)
May 26, 2023
Transfusion-dependent Beta-thalassemia After Gene Therapy
Recruiting
- Transfusion-dependent Beta-Thalassemia
- Gene Therapy
- Gene therapy
-
Tianjin, Tianjin, ChinaRegenerative Medicine Center
Aug 6, 2023
Drive Decision-AIDS for Gene Therapy for Rare Diseases (GENETX)
Not yet recruiting
- Sickle Cell Disease
- Interview
-
Memphis, TennesseeSt. Jude Children's Research Hospital
Mar 30, 2023
Liver Biopsy Following Gene Therapy For Hemophilia
Not yet recruiting
- Hemophilia A
- Hemophilia B
- Liver Biopsy
-
Memphis, TennesseeSt. Jude Children's Research Hospital
Jun 27, 2023
Leber Congenital Amaurosis Trial in Shanghai (HG004)
Recruiting
- Leber Congenital Amaurosis
- HG004
-
Shanghai, Shanghai, ChinaXinhua Hospital affiliated with Shanghai Jiao Tong UniversitySch
Oct 12, 2023
Sensorineural Hearing Loss, Bilateral Trial in Philadelphia (AAVAnc80-hOTOF via Akouos Delivery Device)
Recruiting
- Sensorineural Hearing Loss, Bilateral
- AAVAnc80-hOTOF via Akouos Delivery Device
-
Philadelphia, PennsylvaniaChildren's Hospital of Philadelphia
Apr 18, 2023
Neovascular Age-related Macular Degeneration, Diabetic Macular Edema, Retinal Vein Occlusion Trial in Shanghai (BD311)
Recruiting
- Neovascular Age-related Macular Degeneration
- +2 more
- BD311
-
Shanghai, Shanghai, ChinaEye & ENT Hospital of Fudan University
Aug 22, 2022
Lysosomal Storage Disease, Metachromatic Leukodystrophy Trial in Milan (OTL-200 Gene Therapy)
Active, not recruiting
- Lysosomal Storage Disease
- Metachromatic Leukodystrophy
- OTL-200 Gene Therapy
-
Milan, ItalyOspedale San Raffaele - Telethon Institute for Gene Therapy (OSR
Nov 4, 2022