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subretinal gene therapy

Showing 1 - 25 of >10,000

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Retinitis Pigmentosa Trial in Tuebingen (subretinal injection of rAAV.hPDE6A)

Active, not recruiting
  • Retinitis Pigmentosa
  • subretinal injection of rAAV.hPDE6A
  • Tuebingen, Germany
    Universitätsklinikum Tübingen, Department für Augenheilkunde
Dec 7, 2022

Neovascular Age-related Macular Degeneration Trial (RRG001)

Not yet recruiting
  • Neovascular Age-related Macular Degeneration
  • (no location specified)
Nov 15, 2023

Retinitis Pigmentosa Trial in Pittsburgh, Paris (SPVN06)

Not yet recruiting
  • Retinitis Pigmentosa
  • Pittsburgh, Pennsylvania
  • +1 more
Feb 17, 2023

Biallelic RPE65 Mutation-associated Retinal Dystrophy Trial in Beijing (FT-001 Low Dose, FT-001 Mid Dose, FT-001 High Dose)

Recruiting
  • Biallelic RPE65 Mutation-associated Retinal Dystrophy
  • FT-001 Low Dose
  • +2 more
  • Beijing, Beijing, China
    Peking Union Medical College Hospital
May 11, 2023

Achromatopsia Trial in Tuebingen (rAAV.hCNGA3)

Recruiting
  • Achromatopsia
  • Tuebingen, Germany
    University Hospital Tuebingen, Center for Ophthalmology
Dec 7, 2022

Retinitis Pigmentosa Trial in Stockholm (CPK850)

Recruiting
  • Retinitis Pigmentosa
  • CPK850
  • Stockholm, Sweden
    Novartis Investigative Site
May 16, 2022

LCA5 Trial (AAV8.hLCA5)

Not yet recruiting
  • LCA5
  • AAV8.hLCA5
  • (no location specified)
Nov 22, 2022

Bietti's Crystalline Dystrophy Trial in Beijing (Gene Replacement Therapy by rAAV2/8-hCYP4V2)

Recruiting
  • Bietti's Crystalline Dystrophy
  • Gene Replacement Therapy by rAAV2/8-hCYP4V2
  • Beijing, Beijing, China
    Beijing Tongren Hospital
May 6, 2021

Amaurosis of Leber, Retinal Diseases Trial in Gainesville, Philadelphia (rAAV2-CBSB-hRPE65)

Active, not recruiting
  • Amaurosis of Leber
  • Retinal Diseases
  • rAAV2-CBSB-hRPE65
  • Gainesville, Florida
  • +1 more
Dec 13, 2021

Age-Related Macular Degeneration Trial in Toronto (NG101 AAV gene therapy)

Not yet recruiting
  • Age-Related Macular Degeneration
  • NG101 AAV gene therapy
  • Toronto, Ontario, Canada
    Vitreous Retina Macula Specialists of Toronto
Aug 2, 2023

Neovascular Age-related Macular Degeneration, Wet Macular Degeneration, Wet Age-related Macular Degeneration Trial in United

Recruiting
  • Neovascular Age-related Macular Degeneration
  • +2 more
  • RGX-314
  • Phoenix, Arizona
  • +12 more
Oct 12, 2021

Retinal Disease, Retinitis Pigmentosa Trial in Riyadh (Subretinal administration of rAAV2-VMD2-hMERTKRecombinant

Completed
  • Retinal Disease
  • Retinitis Pigmentosa
  • Subretinal administration of rAAV2-VMD2-hMERTKRecombinant Adeno-Associated Virus
  • Riyadh, Saudi Arabia
    King Khaled Eye Specialist Hospital
Jan 25, 2022

Retinitis Pigmentosa Trial in Nantes (AAV2/5-hPDE6B)

Active, not recruiting
  • Retinitis Pigmentosa
  • AAV2/5-hPDE6B
  • Nantes, France
    Clinique Ophtalmologique, CHU de Nantes
Feb 28, 2022

Age-Related Macular Degeneration Trial in Beijing (KH631)

Not yet recruiting
  • Age-Related Macular Degeneration
  • Beijing, China
    Beijing Tongren Hospital, Capital Medical University
Jan 3, 2023

To Evaluate the Scaling Clinical Study of AAV2-RPE65 Gene Therapy Agent (LX101) in Patients With Congenital Amaurosis (LCA)

Not yet recruiting
  • To Evaluate the Scaling Clinical Study of AAV2-RPE65 Gene Therapy Agent (LX101) in Patients With Congenital Amaurosis (LCA)
  • (no location specified)
Aug 29, 2023

Leber Congenital Amaurosis Trial in Shanghai (HG004)

Recruiting
  • Leber Congenital Amaurosis
  • HG004
  • Shanghai, Shanghai, China
    Xinhua Hospital affiliated with Shanghai Jiao Tong University Sc
Sep 26, 2023

Subjects Who Received Voretigene Neparvovec-rzyl (AAV2-hRPE65v2)

Active, not recruiting
  • Inherited Retinal Dystrophy Due to RPE65 Mutations
  • AAV2-hRPE65v2
  • (no location specified)
Dec 9, 2021

X-linked Retinoschisis Trial (ATSN-201)

Not yet recruiting
  • X-linked Retinoschisis
  • ATSN-201
  • (no location specified)
May 26, 2023

Transfusion-dependent Beta-thalassemia After Gene Therapy

Recruiting
  • Transfusion-dependent Beta-Thalassemia
  • Gene Therapy
  • Gene therapy
  • Tianjin, Tianjin, China
    Regenerative Medicine Center
Aug 6, 2023

Drive Decision-AIDS for Gene Therapy for Rare Diseases (GENETX)

Not yet recruiting
  • Sickle Cell Disease
  • Interview
  • Memphis, Tennessee
    St. Jude Children's Research Hospital
Mar 30, 2023

Liver Biopsy Following Gene Therapy For Hemophilia

Not yet recruiting
  • Hemophilia A
  • Hemophilia B
  • Liver Biopsy
  • Memphis, Tennessee
    St. Jude Children's Research Hospital
Jun 27, 2023

Leber Congenital Amaurosis Trial in Shanghai (HG004)

Recruiting
  • Leber Congenital Amaurosis
  • HG004
  • Shanghai, Shanghai, China
    Xinhua Hospital affiliated with Shanghai Jiao Tong UniversitySch
Oct 12, 2023

Sensorineural Hearing Loss, Bilateral Trial in Philadelphia (AAVAnc80-hOTOF via Akouos Delivery Device)

Recruiting
  • Sensorineural Hearing Loss, Bilateral
  • AAVAnc80-hOTOF via Akouos Delivery Device
  • Philadelphia, Pennsylvania
    Children's Hospital of Philadelphia
Apr 18, 2023

Neovascular Age-related Macular Degeneration, Diabetic Macular Edema, Retinal Vein Occlusion Trial in Shanghai (BD311)

Recruiting
  • Neovascular Age-related Macular Degeneration
  • +2 more
  • BD311
  • Shanghai, Shanghai, China
    Eye & ENT Hospital of Fudan University
Aug 22, 2022

Lysosomal Storage Disease, Metachromatic Leukodystrophy Trial in Milan (OTL-200 Gene Therapy)

Active, not recruiting
  • Lysosomal Storage Disease
  • Metachromatic Leukodystrophy
  • OTL-200 Gene Therapy
  • Milan, Italy
    Ospedale San Raffaele - Telethon Institute for Gene Therapy (OSR
Nov 4, 2022